Rare diseases under evaluation
ORPHA378
ICD-10 G12.2
UMLS C1527336
MedDRA 10040767
Status Under evaluation
ORPHA791
ICD-10 H35.5
UMLS C0035334
MedDRA 10038914
Status Under evaluation
Sickle Cell Disease
Synonym(s) Sickle Cell Anemia
ORPHA232
ICD-10 D57.0 D57.1 D57.2
UMLS C0002895
MedDRA 10040641
Status Under evaluation
Sjögren’s syndrome
Synonym(s) Sicca syndrome
ORPHA803
ICD-10 H35.0
UMLS C0002736
MedDRA 10002026
Status Under evaluation